The GATA1-HS2 Enhancer Allows Persistent and Position-Independent Expression of a β-globin Transgene
Author:
Publisher
Public Library of Science (PLoS)
Subject
Multidisciplinary
Reference51 articles.
1. The cure of thalassemia by bone marrow transplantation.;G Lucarelli;Blood Rev,2002
2. Therapeutic haemoglobin synthesis in beta-thalassaemic mice expressing lentivirus-encoded human beta-globin.;C May;Nature,2000
3. The degree of phenotypic correction of murine beta -thalassemia intermedia following lentiviral-mediated transfer of a human gamma-globin gene is influenced by chromosomal position effects and vector copy number.;DA Persons;Blood,2003
4. Successful correction of the human beta-thalassemia major phenotype using a lentiviral vector.;G Puthenveetil;Blood,2004
5. In vivo selection of genetically modified erythroblastic progenitors leads to long-term correction of beta-thalassemia.;A Miccio;Proc Natl Acad Sci U S A,2008
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