Multicenter Phase 2 Trial of Sirolimus for Tuberous Sclerosis: Kidney Angiomyolipomas and Other Tumors Regress and VEGF- D Levels Decrease

Author:

Dabora Sandra L.,Franz David Neal,Ashwal Stephen,Sagalowsky Arthur,DiMario Francis J.,Miles Daniel,Cutler Drew,Krueger Darcy,Uppot Raul N.,Rabenou Rahmin,Camposano Susana,Paolini Jan,Fennessy Fiona,Lee Nancy,Woodrum Chelsey,Manola Judith,Garber Judy,Thiele Elizabeth A.

Publisher

Public Library of Science (PLoS)

Subject

Multidisciplinary

Reference57 articles.

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4. Tsc2-Rheb signaling regulates EphA-mediated axon guidance.;D Nie;Nat Neurosci,2010

5. Reversal of learning deficits in a Tsc2+/− mouse model of tuberous sclerosis.;D Ehninger;Nat Med,2008

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