Enzyme replacement therapy for treating mucopolysaccharidosis type IVA (Morquio A syndrome): effect and limitations-Reference-Cited by-同舟云学术

Enzyme replacement therapy for treating mucopolysaccharidosis type IVA (Morquio A syndrome): effect and limitations

Published:2015-10-29 Issue:11 Volume:3 Page:1279-1290
ISSN:2167-8707
Container-title:Expert Opinion on Orphan Drugs
language:en
Short-container-title:Expert Opinion on Orphan Drugs

Author:

Tomatsu Shunji,Sawamoto Kazuki,Shimada Tsutomu,Bober Michael B,Kubaski Francyne,Yasuda Eriko,Mason Robert W,Khan Shaukat,Alméciga-Díaz Carlos J,Barrera Luis A,Mackenzie William G,Orii Tadao

Publisher

Informa Healthcare

Subject

Pharmacology (medical),Health Policy,Pharmacology, Toxicology and Pharmaceutics (miscellaneous)

Link

http://www.tandfonline.com/doi/pdf/10.1517/21678707.2015.1086640

Reference85 articles.

1. Impairment of Body Growth in Mucopolysaccharidoses

2. Growth charts for patients with Hunter syndrome

3. Mucopolysaccharidosis Type IVA (Morquio A Disease): Clinical Review and Current Treatment: A Special Review

4. Skeletal dysplasias: Evaluation with impulse oscillometry and thoracoabdominal motion analysis

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