Funder
Pontificia Universidad Javeriana
Colombia Ministerio de Ciencia Tecnología e Innovación
Reference81 articles.
1. Mucopolysaccharidosis IVA: diagnosis, treatment, and management;Sawamoto;Int. J. Mol. Sci.,2020
2. Mucopolysaccharidosis type IVA: clinical features, biochemistry, diagnosis, genetics, and treatment;Sawamoto,2018
3. Lysosomal storage disease overview;Sun;Ann. Transl. Med.,2018
4. Therapeutic options for mucopolysaccharidoses: current and emerging treatments;Sawamoto;Drugs,2019
5. Efficacy and safety of enzyme replacement therapy with BMN 110 (elosulfase alfa) for Morquio A syndrome (mucopolysaccharidosis IVA): a phase 3 randomised placebo-controlled study;Hendriksz;J. Inherit. Metab. Dis.,2014