Gene Editing in Hematopoietic Stem Cells
Author:
Publisher
Springer Nature Singapore
Link
https://link.springer.com/content/pdf/10.1007/978-981-99-7471-9_11
Reference159 articles.
1. Aiuti A et al (2013) Lentiviral hematopoietic stem cell gene therapy in patients with Wiskott-Aldrich syndrome. Science 341:1233151
2. Angelucci E, Pilo F (2016) Management of iron overload before, during, and after hematopoietic stem cell transplantation for thalassemia major. Ann N Y Acad Sci 1368:115–121. https://doi.org/10.1111/nyas.13027
3. Angelucci E et al (2014) Hematopoietic stem cell transplantation in thalassemia major and sickle cell disease: indications and management recommendations from an international expert panel. Haematologica 99:811–820. https://doi.org/10.3324/haematol.2013.099747
4. Antony JS et al (2018) Gene correction of HBB mutations in CD34+ hematopoietic stem cells using Cas9 mRNA and ssODN donors. Mol Cell Pediatr 5:1–7
5. Anzalone AV et al (2019) Search-and-replace genome editing without double-strand breaks or donor DNA. Nature 576:149–157. https://doi.org/10.1038/s41586-019-1711-4
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