Lumacaftor/Ivacaftor: A Review in Cystic Fibrosis
Author:
Publisher
Springer Science and Business Media LLC
Subject
Pharmacology (medical)
Link
http://link.springer.com/content/pdf/10.1007/s40265-016-0611-2.pdf
Reference53 articles.
1. Cystic Fibrosis Foundation. About cystic fibrosis—what is cystic fibrosis? 2016. https://www.cff.org . Accessed 11 Mar 2016.
2. Bosch B, De Boeck K. Searching for a cure for cystic fibrosis. A 25-year quest in a nutshell. Eur J Pediatr. 2016;175(1):1–8.
3. O’Sullivan BP, Freedman SD. Cystic fibrosis. Lancet. 2009;373(9678):1891–904.
4. Galietta LJ. Managing the underlying cause of cystic fibrosis: a future role for potentiators and correctors. Paediatr Drugs. 2013;15(5):393–402.
5. Griesenbach U, Alton EW. Recent advances in understanding and managing cystic fibrosis transmembrane conductance regulator dysfunction. F1000Prime Rep. 2015;7:64.
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