Searching for a cure for cystic fibrosis. A 25-year quest in a nutshell

Author:

Bosch Barbara,De Boeck Kris

Funder

Fonds Wetenschappelijk Onderzoek (BE)

Publisher

Springer Science and Business Media LLC

Subject

Pediatrics, Perinatology, and Child Health

Reference46 articles.

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2. Aurino S, Nigro V (2006) Readthrough strategies for stop codons in Duchenne muscular dystrophy. Acta Myol 25(1):5–12

3. Awatade NT, Uliyakina I, Farinha CM, Clarke LA, Mendes K, Solé A, Pastor J, Ramos MM, Amaral MD (2014) Measurements of functional responses in human primary lung cells as a basis for personalized therapy for cystic fibrosis. EBioMedicine 2(2):147–53

4. Bell SC, De Boeck K, Amaral MD (2015) New pharmacological approaches for cystic fibrosis: promises, progress, pitfalls. Pharmacol Ther 145:19–34

5. Borowitz D, Lubarsky B, Wilschanski M, Munck A, Gelfond D, Bodewes F, Schwarzenberg SJ (2015). Nutritional status improved in cystic fibrosis patients with the G551D mutation after treatment with ivacaftor. PMID: 26250833

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