Validation of a Set of Instruments to Assess Patient- and Caregiver-Oriented Measurements in Spinal Muscular Atrophy: Results of the SMA-TOOL Study-Reference-Cited by-同舟云学术

Validation of a Set of Instruments to Assess Patient- and Caregiver-Oriented Measurements in Spinal Muscular Atrophy: Results of the SMA-TOOL Study

Published:2022-10-21 Issue:1 Volume:12 Page:89-105
ISSN:2193-8253
Container-title:Neurology and Therapy
language:en
Short-container-title:Neurol Ther

Author:

Vázquez-Costa Juan F.,Branas-Pampillón María,Medina-Cantillo Julita,Povedano Mónica,Pitarch-Castellano Inmaculada,López-Lobato Mercedes,Fernández-Ramos Joaquín A.,Lafuente-Hidalgo Miguel,Rojas-García Ricard,Caballero-Caballero José M.,Málaga Ignacio,Eirís-Puñal Jesús,De Lemus Mencía,Cattinari María G.,Cabello-Moruno Rosana,Díaz-Abós Paola,Sánchez-Menéndez Victoria,Rebollo Pablo,Maurino Jorge,Madruga-Garrido Marcos

Funder

Roche España

Publisher

Springer Science and Business Media LLC

Subject

Neurology (clinical),Neurology

Link

https://link.springer.com/content/pdf/10.1007/s40120-022-00411-2.pdf

Reference39 articles.

1. Nance JR. Spinal muscular atrophy. Continuum (Minneap Minn). 2020;26(5):1348–68.

2. Verhaart IEC, Robertson A, Wilson IJ, Aartsma-Rus A, Cameron S, Jones CC, et al. Prevalence, incidence and carrier frequency of 5q-linked spinal muscular atrophy—a literature review. Orphanet J Rare Dis. 2017;12(1):124.

3. Waldrop MA, Kolb SJ. Current Treatment Options in Neurology-SMA Therapeutics. Curr Treat Options Neurol. 2019;21(6):25.