Current Treatment Options in Neurology—SMA Therapeutics
Author:
Publisher
Springer Science and Business Media LLC
Subject
Neurology (clinical)
Link
http://link.springer.com/content/pdf/10.1007/s11940-019-0568-z.pdf
Reference43 articles.
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3. Beattie CE, Kolb SJ. Spinal muscular atrophy: selective motor neuron loss and global defect in the assembly of ribonucleoproteins. Brain Res. 2018;1693(Pt A:92–7. https://doi.org/10.1016/j.brainres.2018.02.022 .
4. Kolb SJ, Coffey CS, Yankey JW, Krosschell K, Arnold WD, Rutkove SB, et al. Natural history of infantile-onset spinal muscular atrophy. Ann Neurol. 2017;82(6):883–91. https://doi.org/10.1002/ana.25101. A longitudinal, prospective description of the natural history of type 1 spinal muscular atrophy.
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