Risdiplam in Patients Previously Treated with Other Therapies for Spinal Muscular Atrophy: An Interim Analysis from the JEWELFISH Study

Author:

Chiriboga Claudia A.,Bruno Claudio,Duong Tina,Fischer Dirk,Mercuri Eugenio,Kirschner Janbernd,Kostera-Pruszczyk Anna,Jaber Birgit,Gorni Ksenija,Kletzl Heidemarie,Carruthers Imogen,Martin Carmen,Warren Francis,Scalco Renata S.,Wagner Kathryn R.,Muntoni Francesco,Deconinck Nicolas,Balikova Irina,Joniau Inge,Tahon Valentine,Wittevrongel Sylvia,Goemans Nathalie,Cassiman Catherine,Prove Lies,Vancampenhout Lisa,van den Hauwe Marleen,Van Impe Annelies,Cances Claude,Soler Vincent,De La Morandais Lauriane Maillard,Vovan Delphine,Cintas Pascal,Auriol Françoise,Mus Marianne,Alphonsa Gwennaelle,Bellio Valerie,Gil Mato Olaia,Flamein Florence,Evrard Cécile,Ziouche Amina,Bouacha-Allou Ikram,Debruyne Philippe,Derlyn Gilles,Defoort Sabine,Leroy Florian,Danjoux Loïc,Desguerre Isabelle,Bremond-Gignac Dominique,Rateuax Maxence,Deladrière Elodie,Vuillerot Carole,Veillerot Quentin,Sibille-Dabadi Bénédicte,Barrière Aurélie,Tinat Marie,Saidi Manel,Fontaine Stephanie,De Montferrand Camille,Le-Goff Laure,Portefaix Aurélie,Louvier Ulrike Walther,Duval Pierre-André,Caradec Pascale,Touati Souad,Herranz Alberto Zamora,Kirschner Janbernd,Bollig Jan,Molnár Fanni,Vogt Sibylle,Pechmann Astrid,Schorling David,Wider Sabine,Kölbel Heike,Schara Ulrike,Braun Frederik,Gangfuss Andrea,Hagenacker Tim,Eckstein Anja,Dekowski Dirk,Oeverhaus Michael,Stoehr Mareile,Andres Barbara,Smuda Karin,Bertini Enrico,D’Amico Adele,Petroni Sergio,Valente Paola,Bonetti Anna Maria,Carlesi Adelina,Mizzoni Irene,Bruno Claudio,Pedemonte Marina,Brolatti Noemi,Priolo Enrico,Rao Giuseppe,Sposetti Lorenza,Morando Simone,Comi Giacomo,Osnaghi Silvia,Minorini Valeria,Abbati Francesca,Fassini Federica,Foà Michaela,Lopopolo Maria Amalia,Magri Francesca,Govoni Alessandra,Meneri Megi,Parente Valeria,Mercuri Eugenio,Antonaci Laura,Pera Maria Carmela,Pane Marika,Amorelli Giulia Maria,Barresi Costanza,D’Amico Guglielmo,Orazi Lorenzo,Coratti Giorgia,De Sanctis Roberto,Vita Giuseppe,Sframeli Maria,Vita Gian Luca,Aragona Pasquale,Inferrera Leandro,Postorino Elisa Imelde,Montanini Daniela,Di Bella Vincenzo,Donato Concetta,Calà Elisabetta,Van der Pol Ludo,Aalbers Jos,de Boer Joke,Imhof Saskia,Cooijmans Pascale,Ruyten Thijs,Van Der Woude Danny,Kostera-Pruszczyk Anna,Klimaszewska Beata,Romańczak Dominika,Gierlak-Wójcicka Zuzanna,Kępa Malwina,Sikorski Adam,Sobieraj Marcin,Lusakowska Anna,Kierdaszuk Biruta,Czeczko Karolina,Fischer Dirk,Henzi Bettina,Gugleta Konstantin,Kusnyerik Akos,Siems Patricia,Akos Sabina,Frei Nora,Seppi Christine,Haschke Christine Wondrusch,Guglieri Michela,Straub Volker,Bell Richard,Nassar Mahmoud,Page Stuart,Clarke Michael Patrick,Regan Aedheen,Mayhew Anna,Lofra Robert Muni,Parasuraman Deepak,Bruschi Simone,Ghauri Abdul-Jabbar,Castle Andrew,Naqvi Saima,Patt Nicola,Scoto Mariacristina,Trucco Federica,Henderson Robert H,Kukadia Roopen,Moore Will,Milev Evelin,Rye Catherine,Selby Victoria,Wolfe Amy,Darras Basil,Baglieri Anna Maria,Fulton Anne,Lucken Courtney,Maczek Elizabeth,Pasternak Amy,Chiriboga Claudia A,Kane Steven,Bautista Ma Edylin M.,Frommer Eileen,Pensec Noelle,Salazar Rachel,Yochai Cara,Rodrigues-Torres Rafael,Chawla Manroop,Day John,Beres Shannon,Gee Richard,Young Sally Dunaway,Finkel Richard,Nazario Aledie Navas,Fasiuddin Airaj,Wells Julie A.,Wilson Jennifer,Berry Debbie,Rizzo Virgina,Duke Julie,Monduy Migvis,Collado Jorge,

Funder

F. Hoffmann-La Roche

Publisher

Springer Science and Business Media LLC

Subject

Neurology (clinical),Neurology

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