Emerging therapies for neurodegenerative lysosomal storage disorders - from concept to reality
Author:
Publisher
Wiley
Subject
Genetics(clinical),Genetics
Link
http://www.springerlink.com/index/pdf/10.1007/s10545-011-9341-5
Reference86 articles.
1. Arfi A, Richard M, Gandolphe C et al. (2010) Storage correction in cells of patients suffering from mucopolysaccharidoses types IIIA and VII after treatment with genistein and other isoflavones. J Inherit Metab Dis 33:61–67
2. Blanz J, Stroobants S, Lüllmann-Rauch R et al. (2008) Reversal of peripheral and central neural storage and ataxia after recombinant enzyme replacement therapy in alpha-mannosidosis mice. Hum Mol Genet 17:3437–3445
3. Boado RJ, Pardridge WM (2010) Genetic engineering of IgG-glucuronidase fusion proteins. J Drug Target 18:205–211
4. Boado RJ, Zhang Y, Zhang Y et al. (2008) Genetic engineering of a lysosomal enzyme fusion protein for targeted delivery across the human blood-brain barrier. Biotechnol Bioeng 99:475–484
5. Boado RJ, Hui EK, Lu JZ et al. (2009) AGT-181: expression in CHO cells and pharmacokinetics, safety, and plasma iduronidase enzyme activity in Rhesus monkeys. J Biotechnol 144:135–141
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