The efficacy of intracerebroventricular idursulfase-beta enzyme replacement therapy in mucopolysaccharidosis II murine model: heparan sulfate in cerebrospinal fluid as a clinical biomarker of neuropathology-Reference-Cited by-同舟云学术

The efficacy of intracerebroventricular idursulfase-beta enzyme replacement therapy in mucopolysaccharidosis II murine model: heparan sulfate in cerebrospinal fluid as a clinical biomarker of neuropathology

Published:2018-07-05 Issue:6 Volume:41 Page:1235-1246
ISSN:0141-8955
Container-title:Journal of Inherited Metabolic Disease
language:en
Short-container-title:J Inherit Metab Dis

Author:

Sohn Young Bae¹,Ko Ah-Ra²³,Seong Mi-ran²,Lee Soyeon²,Kim Mi Ra²,Cho Sung Yoon³,Kim Jung-Sun⁴⁵,Sakaguchi Makoto⁶,Nakazawa Takahiro⁶,Kosuga Motomichi⁷,Seo Joo Hyun⁷,Okuyama Torayuki⁷,Jin Dong-Kyu³

Affiliation:

1. ; Department of Medical Genetics, Ajou University Hospital; Ajou University School of Medicine; Suwon Republic of Korea

2. Research Institute for Future Medicine; Samsung Biomedical Research Center; Seoul Republic of Korea

3. ; Department of Pediatrics, Samsung Medical Center; Sungkyunkwan University School of Medicine; 81, Irwon-ro, Gangnam-gu Seoul 06351 Republic of Korea

4. ; Department of Pathology and Translational Genomics, Samsung Medical Center; Sungkyunkwan University School of Medicine; Seoul Republic of Korea

5. ; Department of Health Sciences and Technology; Sungkyunkwan University; SAIHST Seoul Republic of Korea

6. AnGes, Inc.; Osaka Japan

7. ; Center for Lysosomal Storage Diseases; National Center for Child Health and Development; 2-10-1, Ohkura, Setagaya-ku Tokyo 157-8535 Japan

Funder

AnGes MG, Inc.

Samsung Medical Center

AnGes MG, Inc

Publisher

Wiley

Subject

Genetics(clinical),Genetics