Enzyme augmentation therapy enhances the therapeutic efficacy of bone marrow transplantation in mucopolysaccharidosis type II mice-Reference-Cited by-同舟云学术

Enzyme augmentation therapy enhances the therapeutic efficacy of bone marrow transplantation in mucopolysaccharidosis type II mice

Published:2014-02 Issue:2 Volume:111 Page:139-146
ISSN:1096-7192
Container-title:Molecular Genetics and Metabolism
language:en
Short-container-title:Molecular Genetics and Metabolism

Author:

Akiyama Kazumasa,Shimada Yohta,Higuchi Takashi,Ohtsu Makoto,Nakauchi Hiromitsu,Kobayashi Hiroshi,Fukuda Takahiro,Ida Hiroyuki,Eto Yoshikatsu,Crawford Brett E.,Brown Jillian R.,Ohashi Toya

Funder

Vehicle Racing Commemorative Foundation

Publisher

Elsevier BV

Subject

Endocrinology,Genetics,Molecular Biology,Biochemistry,Endocrinology, Diabetes and Metabolism

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4. Japan Elaprase Treatment (JET) study: idursulfase enzyme replacement therapy in adult patients with attenuated Hunter syndrome (Mucopolysaccharidosis II, MPS II);Okuyama;Mol. Genet. Metab.,2010

5. Long-term, open-labeled extension study of idursulfase in the treatment of Hunter syndrome;Muenzer;Genet. Med.,2011

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