AAV Gene Augmentation Therapy for CRB1-Associated Retinitis Pigmentosa-Reference-Cited by-同舟云学术

AAV Gene Augmentation Therapy for CRB1-Associated Retinitis Pigmentosa

Published:2017-11-30 Issue: Volume: Page:135-151
ISSN:1064-3745
Container-title:Retinal Gene Therapy
language:
Short-container-title:

Author:

Alves C. Henrique,Wijnholds Jan

Publisher

Springer New York

Link

http://link.springer.com/content/pdf/10.1007/978-1-4939-7522-8_10

Reference21 articles.

1. Glybera (2012) http://www.ema.europa.eu/ema/index.jsp?curl=pages/medicines/human/medicines/002145/human_med_001480.jsp&mid=WC0b01ac058001d124 . Accessed 29 Nov 2012

2. Bainbridge JW, Smith AJ, Barker SS et al (2008) Effect of gene therapy on visual function in leber’s congenital amaurosis. N Engl J Med 358:2231–2239

3. MacLaren RE, Groppe M, Barnard AR et al (2014) Retinal gene therapy in patients with choroideremia: initial findings from a phase 1/2 clinical trial. Lancet 383:1129–1137

4. Michalakis S, Mühlfriedel R, Tanimoto N et al (2010) Restoration of cone vision in the CNGA3−/− mouse model of congenital complete lack of cone photoreceptor function. Mol Ther 18:2057–2063

5. Sanofi-Genzyme. Safety and Tolerability Study of AAV2- sFLT01 in Patients With Neovascular Age-Related Macular Degeneration (AMD). http://clinicaltrials.gov/ct2/show/NCT01024998

Cited by 13 articles. 订阅此论文施引文献订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献

1. CRB1-Associated Retinal Dystrophies: Genetics, Clinical Characteristics, and Natural History;American Journal of Ophthalmology;2023-02

2. CRISPR/Cas therapeutic strategies for autosomal dominant disorders;Journal of Clinical Investigation;2022-05-02

3. In Utero Fetal Therapy: Stem Cells, Cell Transplantation, Gene Therapy, and CRISPR-Cas9;Clinical Obstetrics & Gynecology;2021-10-21

4. Gene Therapy in Inherited Retinal Diseases: An Update on Current State of the Art;Frontiers in Medicine;2021-10-15

5. Defining Phenotype, Tropism, and Retinal Gene Therapy Using Adeno-Associated Viral Vectors (AAVs) in New-Born Brown Norway Rats with a Spontaneous Mutation in Crb1;International Journal of Molecular Sciences;2021-03-30