Nusinersen in the Treatment of Spinal Muscular Atrophy
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Publisher
Springer New York
Link
http://link.springer.com/content/pdf/10.1007/978-1-4939-8651-4_4
Reference20 articles.
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3. Kolb SJ, Kissel JT (2015) Spinal muscular atrophy. Neurol Clin 33(4):831–846. https://doi.org/10.1016/j.ncl.2015.07.004
4. Taylor JE et al (1998) Correlation of SMNt and SMNc gene copy number with age of onset and survival in spinal muscular atrophy. Eur J Hum Genet 6:8. https://doi.org/10.1038/sj.ejhg.5200210
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