Nusinersen: The First Option Beyond Supportive Care for Spinal Muscular Atrophy
Author:
Publisher
Springer Science and Business Media LLC
Subject
Pharmacology (medical),General Medicine
Link
http://link.springer.com/article/10.1007/s40261-017-0557-5/fulltext.html
Reference23 articles.
1. Shababi M, Lorson CL, Rudnik-Schoneborn SS. Spinal muscular atrophy: a motor neuron disorder or a multi-organ disease? J. Anat. 2014;224:15–28.
2. d’Ydewalle Constantin, Sumner Charlotte J. Spinal muscular atrophy therapeutics: where do we stand? Neurotherapeutics. 2015;12:303–16.
3. Arnold WD, Kassar D, Kissel JT. Spinal muscular atrophy: diagnosis and management in a new therapeutic era. Muscle Nerve. 2015;51:157–67.
4. Hoy SM. Nusinersen: first global approval. Drugs. 2017. doi: 10.1007/s40265-017-0711-7 .
5. Sullivan DL. Spinraza spinal muscular atrophy. Washington state health care authority. 2017. https://www.hca.wa.gov/assets/program/dur-spinraza-2017-2-22.pdf . Accessed 31 Mar 2017.
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