Nusinersen: First Global Approval
Author:
Publisher
Springer Science and Business Media LLC
Subject
Pharmacology (medical)
Link
http://link.springer.com/content/pdf/10.1007/s40265-017-0711-7.pdf
Reference16 articles.
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2. Farrar MA, Park SB, Vucic S, et al. Emerging therapies and challenges in spinal muscular atrophy. Ann Neurol. 2016. doi: 10.1002/ana.24864 .
3. US National Library of Medicine. Genetics Home Reference: spinal muscular atrophy. 2017. https://ghr.nlm.nih.gov/ . Accessed 16 Jan 2017.
4. Lefebvre S, Burglen L, Reboullet S, et al. Identification and characterization of a spinal muscular atrophy-determining gene. Cell. 1995;80(1):155–65.
5. Garber K. Big win possible for Ionis/Biogen antisense drug in muscular atrophy. Nat Biotech. 2016;34(10):1002–3.
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