Treatment of retinitis pigmentosa due to MERTK mutations by ocular subretinal injection of adeno-associated virus gene vector: results of a phase I trial-Reference-Cited by-同舟云学术

Treatment of retinitis pigmentosa due to MERTK mutations by ocular subretinal injection of adeno-associated virus gene vector: results of a phase I trial

Published:2016-01-29 Issue:3 Volume:135 Page:327-343
ISSN:0340-6717
Container-title:Human Genetics
language:en
Short-container-title:Hum Genet

Author:

Ghazi Nicola G.,Abboud Emad B.,Nowilaty Sawsan R.,Alkuraya Hisham,Alhommadi Abdulrahman,Cai Huimin,Hou Rui,Deng Wen-Tao,Boye Sanford L.,Almaghamsi Abdulrahman,Al Saikhan Fahad,Al-Dhibi Hassan,Birch David,Chung Christopher,Colak Dilek,LaVail Matthew M.,Vollrath Douglas,Erger Kirsten,Wang Wenqiu,Conlon Thomas,Zhang Kang,Hauswirth William,Alkuraya Fowzan S.^ORCID

Funder

King Salman Center for Disaiblity Research

Publisher

Springer Science and Business Media LLC

Subject

Genetics (clinical),Genetics

Link

http://link.springer.com/content/pdf/10.1007/s00439-016-1637-y.pdf

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