Phase-Appropriate Potency Assay Development for AAV-Based Gene Therapy Products
Author:
Publisher
Springer International Publishing
Link
https://link.springer.com/content/pdf/10.1007/978-3-031-28489-2_10
Reference15 articles.
1. Aronson SJ, Bakker RS, Moenis S et al (2020) A quantitative in vitro potency assay for adeno-associated virus vectors encoding for the UGT1A1 transgene. Mol Ther Methods Clin Dev 18:250–258. https://doi.org/10.1016/j.omtm.2020.06.002
2. Ayuso E, Mingozzi F, Bosch F (2010) Production, purification and characterization of AAV. Curr Gene Ther 10:423–436
3. Bishnu P, Chen A, Salami CO et al (2018) In vivo potency assay for adeno-associated virus–based gene therapy vectors using AAVrh.10 as an example. Hum Gene Ther Methods 29(3):146–155. https://doi.org/10.1089/hgtb.2017.246
4. Campomenosi P, Gini E, Noonan DM, Poli A, Rotolo N, Dominioni L, Imperatori A (2016) A comparison between quantitative PCR and droplet digital PCR technologies for circulating microRNA quantification in human lung cancer. BMC Biotechnol 16(1):60
5. Clarner P, Lau SK, Chowdhury T, Guilmette E, Trapa P, Lo SC, Shen S (2021) Development of a one-step RT-ddPCR method to determine the expression and potency of AAV vectors. Mol Ther Methods Clin Dev 23:68–77
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