A Quantitative In Vitro Potency Assay for Adeno-Associated Virus Vectors Encoding for the UGT1A1 Transgene-Reference-Cited by-同舟云学术

A Quantitative In Vitro Potency Assay for Adeno-Associated Virus Vectors Encoding for the UGT1A1 Transgene

Published:2020-09 Issue: Volume:18 Page:250-258
ISSN:2329-0501
Container-title:Molecular Therapy - Methods & Clinical Development
language:en
Short-container-title:Molecular Therapy - Methods & Clinical Development

Author:

Aronson Sem J.,Bakker Robert S.,Moenis Sascha,van Dijk Remco,Bortolussi Giulia,Collaud Fanny,Shi Xiaoxia,Duijst Suzanne,ten Bloemendaal Lysbeth,Ronzitti Giuseppe,Muro Andrés F.,Mingozzi Federico,Beuers Ulrich,Bosma Piter J.

Funder

ZonMw

European Commission

Publisher

Elsevier BV

Subject

Genetics,Molecular Biology,Molecular Medicine

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