RNA-Based Therapeutic Strategies for Inherited Retinal Dystrophies
Author:
Publisher
Springer International Publishing
Link
http://link.springer.com/content/pdf/10.1007/978-3-030-27378-1_12
Reference41 articles.
1. Aartsma-Rus A, Bremmer-Bout M, Janson AA et al (2002) Targeted exon skipping as a potential gene correction therapy for Duchenne muscular dystrophy. Neuromuscul Disord 12(Suppl 1):S71–S77
2. Abudayyeh OO, Gootenberg JS, Essletzbichler P et al (2017) RNA targeting with CRISPR-Cas13. Nature 550:280–284
3. Albert S, Garanto A, Sangermano R et al (2018) Identification and rescue of splice defects caused by two neighboring deep-intronic ABCA4 mutations underlying Stargardt disease. Am J Hum Genet 102:517–527
4. Ameri H (2018) Prospect of retinal gene therapy following commercialization of voretigene neparvovec-rzyl for retinal dystrophy mediated by RPE65 mutation. J Curr Ophthalmol 30:1–2
5. Bass BL, Weintraub H (1987) A developmentally regulated activity that unwinds RNA duplexes. Cell 48:607–613
Cited by 8 articles. 订阅此论文施引文献 订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献
1. Alternative RNA Splicing in the Retina: Insights and Perspectives;Cold Spring Harbor Perspectives in Medicine;2023-01-23
2. Gene-agnostic therapeutic approaches for inherited retinal degenerations;Frontiers in Molecular Neuroscience;2023-01-09
3. A Systematic Review of Artificial Intelligence Applications Used for Inherited Retinal Disease Management;Medicina;2022-03-31
4. Correlating optical coherence tomography biomarkers with visual acuity in nigerian retinitis pigmentosa patients;Nigerian Journal of Clinical Practice;2022
5. Nanotechnology-Based Strategies to Overcome Current Barriers in Gene Delivery;International Journal of Molecular Sciences;2021-08-09
1.学者识别学者识别
2.学术分析学术分析
3.人才评估人才评估
"同舟云学术"是以全球学者为主线，采集、加工和组织学术论文而形成的新型学术文献查询和分析系统，可以对全球学者进行文献检索和人才价值评估。用户可以通过关注某些学科领域的顶尖人物而持续追踪该领域的学科进展和研究前沿。经过近期的数据扩容，当前同舟云学术共收录了国内外主流学术期刊6万余种，收集的期刊论文及会议论文总量共计约1.5亿篇，并以每天添加12000余篇中外论文的速度递增。我们也可以为用户提供个性化、定制化的学者数据。欢迎来电咨询！咨询电话：010-8811{复制后删除}0370
www.globalauthorid.com
TOP
Copyright © 2019-2024 北京同舟云网络信息技术有限公司 京公网安备11010802033243号 京ICP备18003416号-3