1. Adrian R. Krainer 美国 Cold Spring Harbor Laboratory 2019美国医学院院士;2020美国科学院院士;2021沃尔夫医学奖 Antisense Oligonucleotide Therapies for Neurodegenerative Diseases
2. Don W. Cleveland 美国 University of California, San Diego 2006美国科学院院士;2012美国医学院院士 Cryptic splicing of stathmin-2 and UNC13A mRNAs is a pathological hallmark of TDP-43-associated Alzh..
3. Hyman, Bradley T. 美国 Harvard Medical School 2014美国医学院院士 Cryptic splicing of stathmin-2 and UNC13A mRNAs is a pathological hallmark of TDP-43-associated Alzh..
4. Nancy M. Bonini 美国 University of Pennsylvania 2012美国医学院院士;2012美国科学院院士 TDP-43 impairs sleep in Drosophila through Ataxin-2-dependent metabolic disturbance
5. Nancy M. Bonini 美国 University of Pennsylvania 2012美国医学院院士;2012美国科学院院士 m1A in CAG repeat RNA binds to TDP-43 and induces neurodegeneration
6. Roy Parker 美国 University of Colorado Boulder 2012美国科学院院士 Formation, function, and pathology of RNP granules
7. Don W. Cleveland 美国 University of California, San Diego 2006美国科学院院士;2012美国医学院院士 Mechanism of STMN2 cryptic splice-polyadenylation and its correction for TDP-43 proteinopathi..
8. Dawson, Ted M. 美国 Johns Hopkins University School of Medicine 2021美国医学院院士 Poly(ADP-ribose) promotes toxicity of C9ORF72 arginine-rich dipeptide repeat proteins
9. Brown, Robert H. 美国 University of Massachusetts Medical School 2001美国医学院院士 Approaches to Gene Modulation Therapy for ALS
10. Brown, Robert H. 美国 University of Massachusetts Medical School 2001美国医学院院士 Suppression of mutant C9orf72 expression by a potent mixed backbone antisense oligonucleotide
11. Davidson, Beverly L. 美国 University of Pennsylvania School of Medicine 2019美国医学院院士 Gene therapy for ALS: A review
12. Nancy M. Bonini 美国 University of Pennsylvania 2012美国医学院院士;2012美国科学院院士 Toxicity of pathogenic ataxin-2 in Drosophila shows dependence on a pure CAG repeat sequence
13. 顾晓松 中国 南通大学 中国工程院院士 Amyotrophic Lateral Sclerosis: Molecular Mechanisms, Biomarkers, and Therapeutic Strategies
14. VijayRaghavan, Krishnaswamy 印度 Tata Institute of Fundamental Research 2014美国科学院院士 Antagonistic roles for Ataxin-2 structured and disordered domains in RNP condensation
15. 张明杰 中国 南方科技大学 中国科学院院士 Liquid-Liquid Phase Separation in Physiology and Pathophysiology of the Nervous System
16. Don W. Cleveland 美国 University of California, San Diego 2006美国科学院院士;2012美国医学院院士 Antisense Drugs Make Sense for Neurological Diseases
17. Roy Parker 美国 University of Colorado Boulder 2012美国科学院院士 Mechanisms and Regulation of RNA Condensation in RNP Granule Formation
18. Brenner, David A. 美国 University of California, San Diego School of Medicine 2012美国医学院院士 Gene-specific treatment approaches in amyotrophic lateral sclerosis in the present and future
19. St George-Hyslop, PH 加拿大 University of Toronto 2007美国医学院院士 Inherited and Sporadic Amyotrophic Lateral Sclerosis and Fronto-Temporal Lobar Degenerations arising..
20. Don W. Cleveland 美国 University of California, San Diego 2006美国科学院院士;2012美国医学院院士 Cytoplasmic TDP-43 De-mixing Independent of Stress Granules Drives Inhibition of Nuclear Import, Los..