1. 曾溢滔 中国 上海交通大学医学院 中国工程院院士 Gene Editing of the Endogenous Cryptic 3′ Splice Site Corrects the RNA Splicing Defect in the β
2. Jonathan S,Weissman 美国 University of California-San Francisco 2009美国科学院院士 Brainwide silencing of prion protein by AAV-mediated delivery of an engineered compact epigenetic ed..
3. Fussenegger ,Martin 瑞士 ETH Zurich 2017美国工程院院士 Synthetic Gene Circuits for Regulation of Next-Generation Cell-Based Therapeutics
4. Cavazzana, Marina 法国 Paris University Medical School 2019美国医学院院士 Adenine base editor-mediated correction of the common and severe IVS1-110 (G>A) β-thalassemia mu..
5. Blazar, Bruce R. 美国 University of Minnesota, Minneapolis 2012美国医学院院士 Disruption of HIV-1 co-receptors CCR5 and CXCR4 in primary human T cells and hematopoietic stem and ..
6. 刘如谦 美国 Harvard University 2020美国医学院院士;2021美国科学院院士 Disruption of HIV-1 co-receptors CCR5 and CXCR4 in primary human T cells and hematopoietic stem and ..
7. Howard Y. Chang 美国 Stanford University 2017美国医学院院士;2020美国科学院院士 Genome-wide programmable transcriptional memory by CRISPR-based epigenome editing
8. Bradley E,Bernstein 美国 Harvard University 2023美国医学院院士 Genome-wide programmable transcriptional memory by CRISPR-based epigenome editing
9. Jonathan S,Weissman 美国 University of California-San Francisco 2009美国科学院院士 Genome-wide programmable transcriptional memory by CRISPR-based epigenome editing
10. Bradley E,Bernstein 美国 Harvard University 2023美国医学院院士 Epigenome editing strategies for the functional annotation of CTCF insulators
11. 金梅林 中国 华中农业大学 2023中国工程院院士 The prokaryotic Argonaute proteins enhance homology sequence-directed recombination in bacteria
12. 魏于全 中国 四川大学 中国科学院院士 Targeted demethylation of the SARI promotor impairs colon tumour growth
13. 梁锦荣 美国 Columbia University 2013美国工程院院士;2020美国医学院院士 HPV Oncogene Manipulation Using Nonvirally Delivered CRISPR/Cas9 or Natronobacterium gregoryi Argona..
14. George M. Church 美国 Harvard Medical School 2011美国科学院院士;2012美国工程院院士 Beyond editing to writing large genomes
15. Anthony J,Atala 美国 Wake Forest University 2011美国医学院院士 No evidence of genome editing activity from Natronobacterium gregoryi Argonaute (NgAgo) in human cel..
16. Chen, Irvin S. Y. 美国 University of California Los Angeles Excision of HIV-1 Provirus in Human Primary Cells with Nanocapsuled TALEN Proteins
17. 卢云峰 美国 University of California Los Angeles Excision of HIV-1 Provirus in Human Primary Cells with Nanocapsuled TALEN Proteins
18. Alok,Srivastava 印度 Christian Medical College Precise correction of a spectrum of (3-thalassemia mutations in coding and non-coding regions by bas..
19. Xiaodong,Cheng 美国 University of Texas MD Anderson Cancer Center Keep Fingers on the CpG Islands
20. Adam R,Brandt 美国 Stanford University US oil and gas system emissions from nearly one million aerial site measurements