Nusinersen for spinal muscular atrophy
Author:
Publisher
SAGE Publications
Subject
Neurology (clinical),Neurology,Pharmacology
Link
http://journals.sagepub.com/doi/pdf/10.1177/1756285618754459
Reference10 articles.
1. Spinal muscular atrophy
2. Prevalence, incidence and carrier frequency of 5q–linked spinal muscular atrophy – a literature review
3. Results from a phase 1 study of nusinersen (ISIS-SMNRx) in children with spinal muscular atrophy
4. Treatment of infantile-onset spinal muscular atrophy with nusinersen: a phase 2, open-label, dose-escalation study
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