Antisense oligonucleotide therapy reduces seizures and extends life span in an SCN2A gain-of-function epilepsy model
Author:
Funder
National Health and Medical Research Council
RogCon Biosciences
Publisher
American Society for Clinical Investigation
Subject
General Medicine
Link
https://www.jci.org/articles/view/152079/files/pdf
Reference42 articles.
1. ILAE classification of the epilepsies: Position paper of the ILAE Commission for Classification and Terminology
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5. FDA Approves Eteplirsen for Duchenne Muscular Dystrophy: The Next Chapter in the Eteplirsen Saga
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