Gene therapy ameliorates spontaneous seizures associated with cortical neuron loss in a Cln2R207X mouse model-Reference-Cited by-同舟云学术

Gene therapy ameliorates spontaneous seizures associated with cortical neuron loss in a Cln2R207X mouse model

Published:2023-06-15 Issue:12 Volume:133 Page:
ISSN:1558-8238
Container-title:Journal of Clinical Investigation
language:en
Short-container-title:

Author:

Takahashi Keigo^ORCID,Eultgen Elizabeth M.,Wang Sophie H.,Rensing Nicholas R.,Nelvagal Hemanth R.^ORCID,Dearborn Joshua T.^ORCID,Danos Olivier,Buss Nicholas^ORCID,Sands Mark S.,Wong Michael^ORCID,Cooper Jonathan D.^ORCID

Funder

Noah’s Hope/Hope for Bridget

REGENXBIO

Department of Pediatrics, Washington University in St Louis

NIH

McDonnell International Scholars Academy

Washington University in St Louis, McDonnell Center for Systems Neuroscience Small Grant

Publisher

American Society for Clinical Investigation

Subject

General Medicine

Link

https://www.jci.org/articles/view/165908/files/pdf

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