Brain pharmacology of intrathecal antisense oligonucleotides revealed through multimodal imaging-Reference-Cited by-同舟云学术

Brain pharmacology of intrathecal antisense oligonucleotides revealed through multimodal imaging

Published:2019-10-17 Issue:20 Volume:4 Page:
ISSN:2379-3708
Container-title:JCI Insight
language:en
Short-container-title:

Author:

Mazur Curt,Powers Berit,Zasadny Kenneth,Sullivan Jenna M.,Dimant Hemi^ORCID,Kamme Fredrik,Hesterman Jacob,Matson John,Oestergaard Michael,Seaman Marc,Holt Robert W.,Qutaish Mohammed,Polyak Ildiko,Coelho Richard,Gottumukkala Vijay,Gaut Carolynn M.,Berridge Marc,Albargothy Nazira J.^ORCID,Kelly Louise,Carare Roxana O.,Hoppin Jack,Kordasiewicz Holly,Swayze Eric E.,Verma Ajay

Funder

Biogen

Ionis Pharmaceuticals

Publisher

American Society for Clinical Investigation

Subject

General Medicine

Link

https://insight.jci.org/articles/view/129240/files/pdf

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1. Intrathecal administration of nusinersen in adolescent and adult SMA type 2 and 3 patients

2. Treatment of infantile-onset spinal muscular atrophy with nusinersen: a phase 2, open-label, dose-escalation study