Safety and Biological Efficacy of a Lipid–CFTR Complex for Gene Transfer in the Nasal Epithelium of Adult Patients with Cystic Fibrosis-Reference-Cited by-同舟云学术

Safety and Biological Efficacy of a Lipid–CFTR Complex for Gene Transfer in the Nasal Epithelium of Adult Patients with Cystic Fibrosis

Published:2000-01 Issue:1 Volume:1 Page:105-114
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Noone Peadar G.,Hohneker Katherine W.,Zhou Zhaoqing,Johnson Larry G.,Foy Carla,Gipson Clay,Jones Kim,Noah Terry L.,Leigh Margaret W.,Schwartzbach Caryl,Efthimiou John,Pearlman Rodney,Boucher Richard C.,Knowles Michael R.

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference29 articles.

1. Cationic lipid-mediated CFTR gene transfer to the lungs and nose of patients with cystic fibrosis: A double blind placebo-controlled trial;Alton;Lancet,1999

2. Aerosol administration of a recombinant adenovirus expressing CFTR to cystic fibrosis patients: A phase I clinical trial;Bellon;Hum. Gene Ther.,1997

3. Na+ transport in cystic fibrosis epithelia. Abnormal rate and response to adenyl cyclase activation;Boucher;J. Clin. Invest.,1986

4. Liposome mediated CFTR gene transfer to the nasal epithelium of patients with cystic fibrosis;Caplen;Nature Med.,1995

5. Administration of an adenovirus containing the human CFTR cDNA to the respiratory tract of individuals with cystic fibrosis [see comments];Crystal;Nat. Genet.,1994

Cited by 116 articles. 订阅此论文施引文献订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献

1. A new era of targeting cystic fibrosis with non-viral delivery of genomic medicines;Advanced Drug Delivery Reviews;2024-06

2. Molecular and functional correction of a deep intronic splicing mutation in CFTR by CRISPR-Cas9 gene editing;Molecular Therapy - Methods & Clinical Development;2023-12

3. Nanoparticle-Mediated Strategies for Enhanced Drug Penetration and Retention in the Airway Mucosa;Pharmaceutics;2023-10-13

4. Lipid‐based nucleic acid therapeutics with in vivo efficacy;WIREs Nanomedicine and Nanobiotechnology;2022-09-30

5. Gene Therapy: A Possible Alternative to CFTR Modulators?;Frontiers in Pharmacology;2021-04-21