Low-Dose N-Butyldeoxynojirimycin (OGT 918) for Type I Gaucher Disease
Author:
Publisher
Elsevier BV
Subject
Cell Biology,Hematology,Molecular Biology,Molecular Medicine
Reference4 articles.
1. Glucosylceramide lipidoses;Beutler,1995
2. Replacement therapy for inherited enzyme deficiency: Macrophage-targeted glucocerebrosidase for Gaucher's disease;Barton;N. Engl. J. Med.,1991
3. Novel oral treatment of Gaucher's disease with N-butyldeoxynojirimycin (OGT 918) to decrease substrate biosynthesis;Cox;Lancet,2000
4. Treatment of Gaucher's disease with OGT 918;Mistry;Lancet,2000
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