Evaluation of Pathological Manifestations of Disease in Mucopolysaccharidosis VII Mice after Neonatal Hepatic Gene Therapy-Reference-Cited by-同舟云学术

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Evaluation of Pathological Manifestations of Disease in Mucopolysaccharidosis VII Mice after Neonatal Hepatic Gene Therapy

Published:2002-12 Issue:6 Volume:6 Page:745-758
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Xu Lingfei,Mango Robert L.,Sands Mark S.,Haskins Mark E.,Ellinwood N.Matthew,Ponder Katherine Parker

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference47 articles.

1. Prevalence of lysosomal storage disorders;Meikle;JAMA,1999

2. The mucopolysaccharidoses;Neufeld,2001

3. Beta glucuronidase deficiency: Report of clinical, radiologic, and biochemical features of a new mucopolysaccharidosis;Sly;J. Pediatr.,1973

4. Treatment of MPS VII (Sly disease) by allogeneic BMT in a female with homozygous A619V mutation;Yamada;Bone Marrow Transplant.,1998

5. Murine mucopolysaccharidosis type VII: Characterization of a mouse with β-glucuronidase deficiency;Birkenmeier;J. Clin. Invest.,1989

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