Systemic AAV9 gene transfer in adult GM1 gangliosidosis mice reduces lysosomal storage in CNS and extends lifespan-Reference-Cited by-同舟云学术

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Systemic AAV9 gene transfer in adult GM1 gangliosidosis mice reduces lysosomal storage in CNS and extends lifespan

Published:2015-05-10 Issue:15 Volume:24 Page:4353-4364
ISSN:0964-6906
Container-title:Human Molecular Genetics
language:en
Short-container-title:Hum. Mol. Genet.

Author:

Weismann Cara M.,Ferreira Jennifer,Keeler Allison M.,Su Qin,Qui Linghua,Shaffer Scott A.,Xu Zuoshang,Gao Guangping,Sena-Esteves Miguel

Publisher

Oxford University Press (OUP)

Subject

Genetics(clinical),Genetics,Molecular Biology,General Medicine

Link

http://academic.oup.com/hmg/article-pdf/24/15/4353/17262644/ddv168.pdf

Reference53 articles.

1. Generalized Gangliosidosis: Beta-Galactosidase Deficiency

2. Generalized Gangliosidosis

3. Cerebral G M1 -Gangliosidosis: Chemical Pathology of Visceral Organs

4. GM1 gangliosidosis: Review of clinical, molecular, and therapeutic aspects

5. Suzuki Y. Oshima A. Nanba E. (2008), The Online Metabolic and Molecular Bases of Inherited Disease. McGraw Hill, New York, pp. 1–101.

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