A phase I trial of adeno-associated virus serotype 1-γ-sarcoglycan gene therapy for limb girdle muscular dystrophy type 2C-Reference-Cited by-同舟云学术

A phase I trial of adeno-associated virus serotype 1-γ-sarcoglycan gene therapy for limb girdle muscular dystrophy type 2C

Published:2011-01-10 Issue:2 Volume:135 Page:483-492
ISSN:1460-2156
Container-title:Brain
language:en
Short-container-title:

Author:

Herson Serge,Hentati Faycal,Rigolet Aude,Behin Anthony,Romero Norma B.,Leturcq France,Laforêt Pascal,Maisonobe Thierry,Amouri Rim,Haddad Hafedh,Audit Muriel,Montus Marie,Masurier Carole,Gjata Bernard,Georger Christophe,Cheraï Mustapha,Carlier Pierre,Hogrel Jean-Yves,Herson Ariane,Allenbach Yves,Lemoine François M.,Klatzmann David,Sweeney H. Lee,Mulligan Richard C.,Eymard Bruno,Caizergues Didier,Voït Thomas,Benveniste Olivier

Publisher

Oxford University Press (OUP)

Subject

Clinical Neurology

Link

http://academic.oup.com/brain/article-pdf/135/2/483/23036057/awr342.pdf

Reference30 articles.

1. Effect of gene therapy on visual function in Leber's congenital amaurosis;Bainbridge;N Engl J Med,2008

2. Limb-girdle muscular dystrophy 2C: clinical aspects;Ben Hamida;Neuromuscul Disord,1996

3. Prevalence of serum IgG and neutralizing factors against adeno-associated virus (AAV) types 1, 2, 5, 6, 8, and 9 in the healthy population: implications for gene therapy using AAV vectors;Boutin;Hum Gene Ther,2010

4. Sustained transgene expression despite T lymphocyte responses in a clinical trial of rAAV1-AAT gene therapy;Brantly;Proc Natl Acad Sci USA,2009

5. The limb-girdle muscular dystrophies–proposal for a new nomenclature;Bushby;Neuromuscul Disord,1995

Cited by 74 articles. 订阅此论文施引文献订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献

1. Advanced therapeutic approaches in sarcoglycanopathies;Current Opinion in Pharmacology;2024-06

2. Dystrophin and Associated Proteins;Reference Module in Neuroscience and Biobehavioral Psychology;2024

3. Gene therapy for primary myopathies: literature review and prospects;Archives de Pédiatrie;2023-11

4. The ice age – A review on formulation of Adeno-associated virus therapeutics;European Journal of Pharmaceutics and Biopharmaceutics;2023-09

5. Immune Responses to Muscle-Directed Adeno-Associated Viral Gene Transfer in Clinical Studies;Human Gene Therapy;2023-05-01