Cmah-dystrophin deficient mdx mice display an accelerated cardiac phenotype that is improved following peptide-PMO exon skipping treatment

Author:

Betts Corinne A1,McClorey Graham1,Healicon Richard1,Hammond Suzan M1,Manzano Raquel1,Muses Sofia2,Ball Vicky1,Godfrey Caroline1,Merritt Thomas M3,Westering Tirsa1,O’Donovan Liz4,Wells Kim E2,Gait Michael J4,Wells Dominic J2,Tyler Damian1,Wood Matthew J1

Affiliation:

1. Department of Physiology, Anatomy and Genetics, University of Oxford,South Parks Road, Oxford, UK

2. Department of Comparative Biomedical Sciences, Royal Veterinary College,Royal College Street, London NW1 0TU, UK

3. Clinical Biomanufacturing Facility, Nuffield Department of Clinical Medicine, University of Oxford, Old Road, Oxford, UK

4. Medical Research Council, Laboratory of Molecular Biology, Francis Crick Avenue, Cambridge, UK

Funder

British Heart Foundation

BHF Centre of Research Excellence, Oxford

Medical Research Council

Publisher

Oxford University Press (OUP)

Subject

Genetics(clinical),Genetics,Molecular Biology,General Medicine

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