Specific inhibition of myostatin activation is beneficial in mouse models of SMA therapy-Reference-Cited by-同舟云学术

Specific inhibition of myostatin activation is beneficial in mouse models of SMA therapy

Published:2018-11-27 Issue:7 Volume:28 Page:1076-1089
ISSN:0964-6906
Container-title:Human Molecular Genetics
language:en
Short-container-title:

Author:

Long Kimberly K¹,O’Shea Karen M²,Khairallah Ramzi J²,Howell Kelly³,Paushkin Sergey³,Chen Karen S³,Cote Shaun M¹,Webster Micah T¹,Stains Joseph P⁴,Treece Erin¹,Buckler Alan¹,Donovan Adriana¹

Affiliation:

1. Scholar Rock Inc., 620 Memorial Drive, Cambridge, MA

2. Myologica, 10811 Dewey Way East, New Market, MD

3. SMA Foundation, 888 7th Avenue #400, New York, NY

4. Department of Orthopedics, University of Maryland School of Medicine, Baltimore, MD, USA

Funder

SMA Foundation

Scholar Rock to Myologica LLC

Publisher

Oxford University Press (OUP)

Subject

Genetics(clinical),Genetics,Molecular Biology,General Medicine

Link

http://academic.oup.com/hmg/article-pdf/28/7/1076/28073461/ddy382.pdf

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