Oral disease-modifying therapy for adult patients with spinal muscular atrophy type 2
Author:
Publisher
Media Sphere Publishing Group
Subject
Psychiatry and Mental health,Neurology (clinical)
Reference10 articles.
1. Health, wellbeing and lived experiences of adults with SMA: a scoping systematic review
2. Management of Spinal Muscular Atrophy in the Adult Population
3. Nusinersen in adults with 5q spinal muscular atrophy: a non-interventional, multicentre, observational cohort study
4. Nusinersen safety and effects on motor function in adult spinal muscular atrophy type 2 and 3
5. Safety and efficacy of once-daily risdiplam in type 2 and non-ambulant type 3 spinal muscular atrophy (SUNFISH part 2): a phase 3, double-blind, randomised, placebo-controlled trial
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