CRISPR/Cas9-Based Disease Modeling and Functional Correction of Interleukin 7 Receptor Alpha Severe Combined Immunodeficiency in T-Lymphocytes and Hematopoietic Stem Cells-Reference-Cited by-同舟云学术

CRISPR/Cas9-Based Disease Modeling and Functional Correction of Interleukin 7 Receptor Alpha Severe Combined Immunodeficiency in T-Lymphocytes and Hematopoietic Stem Cells

Published:2024-04-01 Issue:7-8 Volume:35 Page:269-283
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Rai Rajeev¹,Steinberg Zohar¹,Romito Marianna¹,Zinghirino Federica¹,Hu Yi-Ting¹,White Nathan¹,Naseem Asma¹,Thrasher Adrian J.¹²^ORCID,Turchiano Giandomenico¹,Cavazza Alessia¹²³^ORCID

Affiliation:

1. Infection, Immunity, and Inflammation Teaching and Research Department, Great Ormond Street Institute of Child Health, University College London, London, United Kingdom.

2. NIHR Great Ormond Street Hospital Biomedical Research Center, London, United Kingdom.

3. Department of Medical and Surgical Sciences for Children and Adults, University of Modena and Reggio Emilia School of Medicine, Modena, Italy.

Publisher

Mary Ann Liebert Inc

Link

https://www.liebertpub.com/doi/pdf/10.1089/hum.2023.100

Reference49 articles.

1. Severe combined immunodeficiencies (SCID)

2. Interleukin-7 receptor expression: intelligent design

3. Intrathymic IL-7: The where, when, and why of IL-7 signaling during T cell development

4. Interleukin 7 independent development of human B cells.

5. The Earliest T Lineage–Committed Cells Depend on IL-7 for Bcl-2 Expression and Normal Cell Cycle Progression

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