Split AAV8 Mediated ABCA4 Expression for Gene Therapy of Mouse Stargardt Disease (STGD1)-Reference-Cited by-同舟云学术

Split AAV8 Mediated ABCA4 Expression for Gene Therapy of Mouse Stargardt Disease (STGD1)

Published:2023-07-01 Issue:13-14 Volume:34 Page:616-628
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Li Ruiting¹,Jing Qiuping¹,She Kaiqin²,Wang Qingnan³,Jin Xiu¹,Zhao Qinyu¹,Su Jing¹,Song Li¹,Fu Jiamei¹,Wu Xiaoyi¹,Xu Qiuxia¹,Lu Fang²,Wei Yuquan¹,Yang Yang¹²^ORCID

Affiliation:

1. State Key Laboratory of Biotherapy and Cancer Center, West China Hospital, Sichuan University and Collaborative Innovation Center, Chengdu, China

2. Department of Ophthalmology, West China Hospital, Sichuan University, Chengdu, China; and

3. Chengdu Genevector Therapeutics, Inc., Chengdu, China.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

https://www.liebertpub.com/doi/pdf/10.1089/hum.2023.017

Reference49 articles.

1. Natural History of Phenotypic Changes in Stargardt Macular Dystrophy

2. Clinically Focused Molecular Investigation of 1000 Consecutive Families with Inherited Retinal Disease

3. Light exposure stimulates formation of A2E oxiranes in a mouse model of Stargardt's macular degeneration

4. Defective lipid transport and biosynthesis in recessive and dominant Stargardt macular degeneration

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