The Role of Conditioning in Hematopoietic Stem-Cell Gene Therapy
Author:
Affiliation:
1. San Raffaele Telethon Institute for Gene Therapy, SR-TIGET; Pediatric Immunohematology, San Raffaele Scientific Institute, Milan, Italy
2. Vita-Salute San Raffaele University, Milan, Italy.
Publisher
Mary Ann Liebert Inc
Subject
Genetics,Molecular Biology,Molecular Medicine
Link
http://www.liebertpub.com/doi/pdf/10.1089/hum.2016.103
Reference48 articles.
1. Clinical Applications of Gene Therapy for Primary Immunodeficiencies
2. Lentiviral Hematopoietic Stem Cell Gene Therapy in Patients with Wiskott-Aldrich Syndrome
3. Hematopoietic Stem Cell Gene Therapy with a Lentiviral Vector in X-Linked Adrenoleukodystrophy
4. Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia
5. Gene therapy returns to centre stage
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