Gene Therapy: The View from NCATS-Reference-Cited by-同舟云学术

Gene Therapy: The View from NCATS

Published:2016-01 Issue:1 Volume:27 Page:7-13
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Brooks Philip J.¹,Yang N. Nora²,Austin Christopher P.³

Affiliation:

1. Division of Clinical Innovation and Office of Rare Diseases Research, National Center for Advancing Translational Sciences (NCATS), National Institutes of Health, Bethesda, Maryland.

2. Division of Preclinical Innovation, National Center for Advancing Translational Sciences (NCATS), National Institutes of Health, Bethesda, Maryland.

3. Office of the Director, National Center for Advancing Translational Sciences (NCATS), National Institutes of Health, Bethesda, Maryland.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/hum.2016.29018.pjb

Reference46 articles.

1. The NCGC Pharmaceutical Collection: A Comprehensive Resource of Clinically Approved Drugs Enabling Repurposing and Chemical Genomics

2. Expanding rare disease drug trials based on shared molecular etiology

3. Gene Therapy for Rare Diseases: Summary of a National Institutes of Health Workshop, September 13, 2012

4. The NIH Extracellular RNA Communication Consortium

5. Hydrophobically Modified siRNAs Silence Huntingtin mRNA in Primary Neurons and Mouse Brain

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