Central Nervous System Delivery of Helper-Dependent Canine Adenovirus Corrects Neuropathology and Behavior in Mucopolysaccharidosis Type VII Mice-Reference-Cited by-同舟云学术

Central Nervous System Delivery of Helper-Dependent Canine Adenovirus Corrects Neuropathology and Behavior in Mucopolysaccharidosis Type VII Mice

Published:2014-03 Issue:3 Volume:25 Page:199-211
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Ariza Lorena¹,Giménez-Llort Lydia²,Cubizolle Aurélie³,Pagès Gemma¹,García-Lareu Belén¹,Serratrice Nicolas³,Cots Dan¹,Thwaite Rosemary¹,Chillón Miguel¹⁴,Kremer Eric J.³,Bosch Assumpció¹

Affiliation:

1. Center of Animal Biotechnology and Gene Therapy and Department of Biochemistry and Molecular Biology, School of Medicine, Universitat Autònoma de Barcelona, 08193 Bellaterra, Barcelona, Spain.

2. Institute of Neuroscience and Department of Psychiatry and Forensic Medicine, School of Medicine, Universitat Autònoma de Barcelona, 08193 Bellaterra, Barcelona, Spain.

3. Institut de Génétique Moléculaire de Montpellier, Université de Montpellier 1 & 2, 34293 Montpellier, France.

4. Institut Català de Recerca i Estudis Avançats, 08193 Barcelona, Spain.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/hum.2013.152

Reference51 articles.

1. Murine mucopolysaccharidosis type VII. Characterization of a mouse with beta-glucuronidase deficiency.

2. Long-Term and Significant Correction of Brain Lesions in Adult Mucopolysaccharidosis Type VII Mice Using Recombinant AAV Vectors

3. Reversal of Pathology in the Entire Brain of Mucopolysaccharidosis Type VII Mice after Lentivirus-Mediated Gene Transfer