Evaluation of Photoreceptor Transduction Efficacy of Capsid-Modified Adeno-Associated Viral Vectors Following Intravitreal and Subretinal Delivery in Sheep-Reference-Cited by-同舟云学术

Evaluation of Photoreceptor Transduction Efficacy of Capsid-Modified Adeno-Associated Viral Vectors Following Intravitreal and Subretinal Delivery in Sheep

Published:2020-07-01 Issue:13-14 Volume:31 Page:719-729
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Ross Maya¹,Obolensky Alexey²,Averbukh Edward²,Ezra-Elia Raaya¹,Yamin Esther²,Honig Hen³,Dvir Hay³,Rosov Alexander³,Hauswirth William W.⁴,Gootwine Elisha³,Banin Eyal²,Ofri Ron¹

Affiliation:

1. Koret School of Veterinary Medicine, The Hebrew University of Jerusalem, Rehovot, Israel.

2. Department of Ophthalmology, Hadassah-Hebrew University Medical Center, Jerusalem, Israel.

3. Agricultural Research Organization, The Volcani Center, Rishon LeZion, Israel.

4. Department of Ophthalmology, University of Florida, Gainesville, Florida, USA.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

https://www.liebertpub.com/doi/pdf/10.1089/hum.2020.023

Reference38 articles.

1. Let There Be Light: Gene and Cell Therapy for Blindness

2. A novel day blindness in sheep: Epidemiological, behavioural, electrophysiological and histopathological studies

3. A mutation in gene CNGA3 is associated with day blindness in sheep

4. Flicker cone function in normal and day blind sheep: a large animal model for human achromatopsia caused by CNGA3 mutation

5. Gene Augmentation Therapy Restores Retinal Function and Visual Behavior in a Sheep Model of CNGA3 Achromatopsia

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