Utility of Self-Destructing CRISPR/Cas Constructs for Targeted Gene Editing in the Retina-Reference-Cited by-同舟云学术

Utility of Self-Destructing CRISPR/Cas Constructs for Targeted Gene Editing in the Retina

Published:2019-11-01 Issue:11 Volume:30 Page:1349-1360
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Li Fan¹²³,Hung Sandy S.C.²,Mohd Khalid Mohd Khairul Nizam¹,Wang Jiang-Hui²⁴,Chrysostomou Vicki²⁴,Wong Vickie H.Y.⁵,Singh Vikrant¹,Wing Kristof¹,Tu Leilei⁶,Bender James A.⁷,Pébay Alice²⁴⁸,King Anna E.⁷,Cook Anthony L.⁷,Wong Raymond C.B.²⁴,Bui Bang V.⁵,Hewitt Alex W.¹²⁴,Liu Guei-Sheung¹²⁴⁶

Affiliation:

1. Menzies Institute for Medical Research, University of Tasmania, Hobart, Australia.

2. Centre for Eye Research Australia, Royal Victorian Eye and Ear Hospital, East Melbourne, Australia.

3. State Key Laboratory of Ophthalmology, Zhongshan Ophthalmic Centre, Sun Yat-sen University, Guangzhou, China.

4. Ophthalmology, Department of Surgery, University of Melbourne, East Melbourne, Australia.

5. Department of Optometry and Vision Sciences, University of Melbourne, Parkville, Australia.

6. Department of Ophthalmology, Jinan University, Guangzhou, China.

7. Wicking Dementia Research and Education Centre, University of Tasmania, Hobart, Australia.

8. Department of Anatomy and Neuroscience, University of Melbourne, Parkville, Australia.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

https://www.liebertpub.com/doi/pdf/10.1089/hum.2019.021

Reference34 articles.

1. Next‐generation genetic testing for retinitis pigmentosa

2. Genetic architecture of retinal and macular degenerative diseases: the promise and challenges of next-generation sequencing

3. Long-Term Effect of Gene Therapy on Leber’s Congenital Amaurosis

4. Improvement and Decline in Vision with Gene Therapy in Childhood Blindness

5. Gene therapy for visual loss: Opportunities and concerns

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