1. School of Bioengineering, East China University of Science and Technology, Shanghai, China
2. School of Pharmacy, East China University of Science and Technology, Shanghai, China
3. Department of Hematology, Clinical Medical College, Yangzhou University, Yangzhou, China
4. Gene Therapy Center, University of North Carolina, Chapel Hill, North Carolina
5. Harold R. Roberts Comprehensive Hemophilia Diagnosis and Treatment Center, University of North Carolina, Chapel Hill, North Carolina
6. Spark Therapeutics, Philadelphia, Pennsylvania
7. Division of Molecular Pharmaceutics, Eshelman School of Pharmacy, University of North Carolina, Chapel Hill, North Carolina.