Long-Term Correction of Copper Metabolism in Wilson's Disease Mice with AAV8 Vector Delivering Truncated ATP7B-Reference-Cited by-同舟云学术

Long-Term Correction of Copper Metabolism in Wilson's Disease Mice with AAV8 Vector Delivering Truncated ATP7B

Published:2019-12-01 Issue:12 Volume:30 Page:1494-1504
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Leng Yingying¹,Li Ping²,Zhou Lifang¹,Xiao Lin²,Liu Yu²,Zheng Zhaoyue²,Qin Fengming¹,Hao Qiukui²,Xu Heng²,Yao Shaohua¹,Dong Biao²

Affiliation:

1. State Key Laboratory of Biotherapy and Cancer Center, West China Hospital, Sichuan University, Chengdu, Sichuan, China.

2. National Clinical Research Center for Geriatrics, State Key Laboratory of Biotherapy, West China Hospital, Sichuan University, Chengdu, Sichuan, China.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

https://www.liebertpub.com/doi/pdf/10.1089/hum.2019.148

Reference46 articles.

1. Wilson Disease: Genetic Basis of Copper Toxicity and Natural History

2. Biological functions of ceruloplasmin and their deficiency caused by mutation in genes regulating copper and iron metabolism

3. Copper Transport in Mammalian Cells: Special Care for a Metal with Special Needs

4. Wilson Disease: Pathogenesis and Clinical Considerations in Diagnosis and Treatment

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