Improved Efficacy and Reduced Toxicity by Ultrasound-Guided Intrahepatic Injections of Helper-Dependent Adenoviral Vector in Gunn Rats-Reference-Cited by-同舟云学术

Improved Efficacy and Reduced Toxicity by Ultrasound-Guided Intrahepatic Injections of Helper-Dependent Adenoviral Vector in Gunn Rats

Published:2013-10 Issue:5 Volume:24 Page:321-327
ISSN:1946-6536
Container-title:Human Gene Therapy Methods
language:en
Short-container-title:Human Gene Therapy Methods

Author:

Pastore Nunzia¹,Nusco Edoardo¹,Piccolo Pasquale¹,Castaldo Sigismondo²,Vaníkova Jana³,Vetrini Francesco⁴,Palmer Donna J.⁴,Vitek Libor³⁵,Ng Philip⁴,Brunetti-Pierri Nicola¹⁶

Affiliation:

1. Telethon Institute of Genetics and Medicine, Naples 80131, Italy.

2. Centro di Biotecnologie, Ospedale Cardarelli, Naples 80131, Italy.

3. Institute of Medical Biochemistry and Laboratory Medicine, 1st Faculty of Medicine, Charles University in Prague, Prague 12808, Czech Republic.

4. Department of Molecular and Human Genetics, Baylor College of Medicine, Houston, TX 77030.

5. 4th Department of Internal Medicine, 1st Faculty of Medicine, Charles University in Prague, Prague 12808, Czech Republic.

6. Department of Translational Medicine, Federico II University of Naples, Naples 80131, Italy.

Publisher

Mary Ann Liebert Inc

Subject

Genetics(clinical),Pharmacology,Genetics,Applied Microbiology and Biotechnology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/hgtb.2013.108

Reference35 articles.

1. Cell‐specific expression of cytosolic phosphoenolpyruvate carboxykinase in transgenic mice

2. Gene therapy for inborn errors of liver metabolism

3. Progress and prospects: gene therapy for genetic diseases with helper-dependent adenoviral vectors

4. Progress Towards Liver and Lung-Directed Gene Therapy with Helper- Dependent Adenoviral Vectors

5. Helper-dependent adenoviral vectors for liver-directed gene therapy

Cited by 11 articles. 订阅此论文施引文献订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献

1. Genetic-Based Approaches to Inherited Metabolic Liver Diseases;Human Gene Therapy;2019-10-01

2. Gene Therapy in Pediatric Liver Disease;Pediatric Hepatology and Liver Transplantation;2019

3. Advances in understanding disease mechanisms and potential treatments for Crigler–Najjar syndrome;Expert Opinion on Orphan Drugs;2018-07-03

4. Crigler-Najjar Syndrome: Current Perspectives and the Application of Clinical Genetics;Endocrine, Metabolic & Immune Disorders - Drug Targets;2018-04-02

5. Helper-Dependent Adenoviral Vectors for Gene Therapy of Inherited Diseases;Safety and Efficacy of Gene-Based Therapeutics for Inherited Disorders;2017