Human miR223 Promoter as a Novel Myelo-Specific Promoter for Chronic Granulomatous Disease Gene Therapy

Author:

Brendel Christian1,Hänseler Walther2,Wohlgensinger Vital2,Bianchi Matteo2,Tokmak Serap1,Chen-Wichmann Linping1,Kuzmenko Elena2,Cesarovic Nikola3,Nicholls Flora4,Reichenbach Janine2,Seger Reinhard2,Grez Manuel1,Siler Ulrich2

Affiliation:

1. Biomedical Research Institute Georg-Speyer-Haus, 60596 Frankfurt, Germany.

2. Division of Immunology/Hematology/BMT, Children's Research Center (CRC), University Children's Hospital Zürich, CH-8032 Zürich, Switzerland.

3. Division of Surgical Research, University Hospital Zürich, CH-8091 Zürich, Switzerland.

4. Central Biological Laboratory, University Hospital Zürich, CH-8091 Zürich, Switzerland.

Publisher

Mary Ann Liebert Inc

Subject

Genetics(clinical),Pharmacology,Genetics,Applied Microbiology and Biotechnology,Molecular Medicine

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