Retrovirus Vector-Mediated Correction and Cross-Correction of Lysosomal alpha-Mannosidase Deficiency in Human and Feline Fibroblasts
Author:
Publisher
Mary Ann Liebert Inc
Subject
Genetics,Molecular Biology,Molecular Medicine
Link
http://www.liebertpub.com/doi/pdf/10.1089/10430349950017996
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1. Lymphocytes transfer only the lysosomal form of α-d-mannosidase during cell-to-cell contact
2. The substrate-specificity of human lysosomal α-d-mannosidase in relation to genetic α-mannosidosis
3. Increased life span and correction of metabolic defects in murine mucopolysaccharidosis type VII after syngeneic bone marrow transplantation
4. Metabolic correction and cross-correction of mucopolysaccharidosis type II (Hunter syndrome) by retroviral-mediated gene transfer and expression of human iduronate-2-sulfatase.
5. Biochemical studies on a case of feline mannosidosis
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