Correction of Enzymatic and Lysosomal Storage Defects in Fabry Mice by Adenovirus-Mediated Gene Transfer-Reference-Cited by-同舟云学术

Correction of Enzymatic and Lysosomal Storage Defects in Fabry Mice by Adenovirus-Mediated Gene Transfer

Published:1999-07 Issue:10 Volume:10 Page:1667-1682
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Ziegler Robin J.,Yew Nelson S.,Li Chester,Cherry Maribeth,Berthelette Patricia,Romanczuk Helen,Ioannou Yiannis A.,Zeidner Kenneth M.,Desnick Robert J.,Cheng Seng H.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/10430349950017671

Reference64 articles.

1. Characterization of an Adenovirus Gene Transfer Vector Containing an E4 Deletion

2. Effect of the E4 region on the persistence of transgene expression from adenovirus vectors

3. Replacement Therapy for Inherited Enzyme Deficiency — Macrophage-Targeted Glucocerebrosidase for Gaucher's Disease

4. Human alpha-galactosidase A: nucleotide sequence of a cDNA clone encoding the mature enzyme.

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