Bone Marrow Stromal Cell-Mediated Gene Therapy for Hemophilia A: In Vitro Expression of Human Factor VIII with High Biological Activity Requires the Inclusion of the Proteolytic Site at Amino Acid 1648-Reference-Cited by-同舟云学术

Bone Marrow Stromal Cell-Mediated Gene Therapy for Hemophilia A: In Vitro Expression of Human Factor VIII with High Biological Activity Requires the Inclusion of the Proteolytic Site at Amino Acid 1648

Published:1999-01 Issue:1 Volume:10 Page:61-76
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Chiang Gisela G.,Rubin Hillard L.,Cherington Van,Mcgrath Claire A.,Gaffney Anita,Levine Peter H.,Greenberger Joel S.,Wang Ti,Sobolewski Joyce,Emami Shahin,Sarver Nava,Hurwitz David R.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/10430349950019192

Reference47 articles.

1. Design and operation of a recombinant mammalian cell manufacturing process for rFVIII

2. Isolation and characterization of human factor VIII: molecular forms in commercial factor VIII concentrate, cryoprecipitate, and plasma.

3. Second Generation, B-Domain Deleted Recombinant Factor VIII

4. Structural and functional characterization of Factor VIII-Δ II, a new recombinant Factor VIII lacking most of the B-domain

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