Safety and Efficacy of AAV5 Vectors Expressing Human or Canine CNGB3 in CNGB3-Mutant Dogs-Reference-Cited by-同舟云学术

Safety and Efficacy of AAV5 Vectors Expressing Human or Canine CNGB3 in CNGB3-Mutant Dogs

Published:2017-12 Issue:4 Volume:28 Page:197-207
ISSN:2324-8637
Container-title:Human Gene Therapy Clinical Development
language:en
Short-container-title:Human Gene Therapy Clinical Development

Author:

Ye Guo-jie¹,Komáromy András M.²³,Zeiss Caroline⁴,Calcedo Roberto³,Harman Christine D.²,Koehl Kristin L.²,Stewart Gabriel A.²,Iwabe Simone³,Chiodo Vince A.⁵,Hauswirth William W.⁵,Aguirre Gustavo D.³,Chulay Jeffrey D.¹

Affiliation:

1. Applied Genetic Technologies Corporation (AGTC), Alachua, Florida

2. College of Veterinary Medicine, Michigan State University, East Lansing, Michigan

3. School of Veterinary Medicine, University of Pennsylvania, Philadelphia, Pennsylvania

4. Yale University Medical School, New Haven, Connecticut

5. University of Florida, Gainesville, Florida.

Publisher

Mary Ann Liebert Inc

Subject

Genetics (clinical)

Link

http://www.liebertpub.com/doi/pdf/10.1089/humc.2017.125

Reference35 articles.

1. KohlS, JagleH, SharpeLT, et al. Achromatopsia. In: PagonRA, BirdTC, DolanCR, StephensK, eds. Gene Reviews [Internet]. Seattle, WA: University of Washington.

2. CNGB3 mutations account for 50% of all cases with autosomal recessive achromatopsia

3. CNGA3 Mutations in Hereditary Cone Photoreceptor Disorders

4. Mutations in the Cone Photoreceptor G-Protein α-Subunit Gene GNAT2 in Patients with Achromatopsia

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